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Development of antisense U1 snRNA-mediated therapeutic strategies to modulate splicing in lysosomal storage disorders

dc.contributor.authorMatos, Liliana
dc.date.accessioned2018-03-29T10:56:07Z
dc.date.available2018-03-29T10:56:07Z
dc.date.issued2017-03-22
dc.description.abstractShort term scientific mission about therapeutic strategies to modulate splicing in lysosomal storage disorders.pt_PT
dc.description.sponsorshipCOST ACTION BM1207pt_PT
dc.description.versionN/Apt_PT
dc.identifier.urihttp://hdl.handle.net/10400.18/5488
dc.language.isoengpt_PT
dc.peerreviewednopt_PT
dc.subjectU1snRNA Splicing Therapiespt_PT
dc.subjectLentiviral Transductionpt_PT
dc.subjectLysosomal Storage Disorderspt_PT
dc.subjectDoenças Genéticaspt_PT
dc.titleDevelopment of antisense U1 snRNA-mediated therapeutic strategies to modulate splicing in lysosomal storage disorderspt_PT
dc.typelecture
dspace.entity.typePublication
oaire.citation.conferencePlacePorto, Portugalpt_PT
oaire.citation.titleCOST (European Cooperation in Science & Technology) Action BM1207 Porto meeting, 22 March 2017pt_PT
rcaap.rightsopenAccesspt_PT
rcaap.typelecturept_PT

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