| Name: | Description: | Size: | Format: | |
|---|---|---|---|---|
| 2.2 MB | Adobe PDF |
Authors
Advisor(s)
Abstract(s)
Short term scientific mission about therapeutic strategies to modulate splicing in lysosomal storage disorders.
Description
Keywords
U1snRNA Splicing Therapies Lentiviral Transduction Lysosomal Storage Disorders Doenças Genéticas
