Repository logo
 
Loading...
Thumbnail Image
Publication

Development of antisense U1 snRNA-mediated therapeutic strategies to modulate splicing in lysosomal storage disorders

Use this identifier to reference this record.
Name:Description:Size:Format: 
STSM COST presentation Matos L, 2017.pdf2.2 MBAdobe PDF Download

Advisor(s)

Abstract(s)

Short term scientific mission about therapeutic strategies to modulate splicing in lysosomal storage disorders.

Description

Keywords

U1snRNA Splicing Therapies Lentiviral Transduction Lysosomal Storage Disorders Doenças Genéticas

Pedagogical Context

Citation

Research Projects

Organizational Units

Journal Issue