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Development of a U1 snRNA-adapted gene therapeutic strategy to correct 5’ splicing defects in lysosomal storage disorders

dc.contributor.authorMatos, Liliana
dc.contributor.authorAlves, Sandra
dc.date.accessioned2016-03-03T18:15:20Z
dc.date.available2016-05-01T00:30:11Z
dc.date.issued2015-03-19
dc.description.sponsorshipLM was supported by a Grant (SFRH/BD/64592/2009)pt_PT
dc.identifier.urihttp://hdl.handle.net/10400.18/3607
dc.language.isoengpt_PT
dc.peerreviewedyespt_PT
dc.subjectDoenças Genéticaspt_PT
dc.subjectU1snRNA therapypt_PT
dc.subjectLysosomal Storage Disorderspt_PT
dc.subjectMPS III Cpt_PT
dc.subjectML III alpha/betapt_PT
dc.subjectMPS Ipt_PT
dc.titleDevelopment of a U1 snRNA-adapted gene therapeutic strategy to correct 5’ splicing defects in lysosomal storage disorderspt_PT
dc.typeconference object
dspace.entity.typePublication
oaire.citation.conferencePlacePorto, Portugalpt_PT
oaire.citation.title11th International Symposium SPDM, 19 março 2015pt_PT
rcaap.rightsrestrictedAccesspt_PT
rcaap.typeconferenceObjectpt_PT

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