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Coutinho et al. Less Is More: Substrate Reduction Therapy for Lysosomal Storage Disorders. Int. J. Mol. Sci. 2016, 17, 1065

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Erratum for Less Is More: Substrate Reduction Therapy for Lysosomal Storage Disorders. [Int J Mol Sci. 2016]

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Gaucher Disease Niemann-Pick type C Sanfilippo Syndrome Combination Ttherapy Eligluistat Tartrate Genistein Miglustat Mucopolysaccharidosis Type III (MPS III; substrate reduction therapy (SRT) Doenças Genéticas

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Int J Mol Sci. 2017 Jan 17;18(1). pii: E178. doi: 10.3390/ijms18010178.

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