| Name: | Description: | Size: | Format: | |
|---|---|---|---|---|
| 137.71 KB | Adobe PDF |
Advisor(s)
Abstract(s)
n/a.
Description
Erratum for Less Is More: Substrate Reduction Therapy for Lysosomal Storage Disorders. [Int J Mol Sci. 2016]
Keywords
Gaucher Disease Niemann-Pick type C Sanfilippo Syndrome Combination Ttherapy Eligluistat Tartrate Genistein Miglustat Mucopolysaccharidosis Type III (MPS III; substrate reduction therapy (SRT) Doenças Genéticas
Pedagogical Context
Citation
Int J Mol Sci. 2017 Jan 17;18(1). pii: E178. doi: 10.3390/ijms18010178.
