Coutinho et al. Less Is More: Substrate Reduction Therapy for Lysosomal Storage Disorders. Int. J. Mol. Sci. 2016, 17, 1065

Coutinho, Maria FranciscaSantos, Juliana InêsAlves, Sandra2018-03-222018-03-222017-01-17Int J Mol Sci. 2017 Jan 17;18(1). pii: E178. doi: 10.3390/ijms18010178.1661-6596http://hdl.handle.net/10400.18/5433Erratum for Less Is More: Substrate Reduction Therapy for Lysosomal Storage Disorders. [Int J Mol Sci. 2016]n/a.engGaucher DiseaseNiemann-Pick type CSanfilippo SyndromeCombination TtherapyEligluistat TartrateGenisteinMiglustatMucopolysaccharidosis Type III (MPS III; substrate reduction therapy (SRT)Doenças GenéticasCoutinho et al. Less Is More: Substrate Reduction Therapy for Lysosomal Storage Disorders. Int. J. Mol. Sci. 2016, 17, 1065journal article10.3390/ijms18010178