New models for the most frequent Mucolipidosis II-causing mutation using iPSCs and zebrafish: a crucial step towards the development of new therapies

2026-01-232026-01-23http://hdl.handle.net/10400.18/10754CRISPR/Cas9,lysosomal storage disorder,in vitro model,in vivo model, Medical and health sciencesNew models for the most frequent Mucolipidosis II-causing mutation using iPSCs and zebrafish: a crucial step towards the development of new therapiesModellingMLII